Vertex and CRISPR Therapeutics Announce US FDA Approval of CASGEVY …
WEBDec 8, 2023 · Vertex leads global development, manufacturing and commercialization of CASGEVY with support from CRISPR Therapeutics. In conjunction with the FDA approval of CASGEVY, Vertex will make a $200 million milestone payment to CRISPR, which will be capitalized and amortized to cost of sales.
FDA Approves First Gene Therapies to Treat Patients with Sickle …
WEBCasgevy, a cell-based gene therapy, is approved for the treatment of sickle cell disease in patients 12 years of age and older with recurrent vaso-occlusive crises. Casgevy is the first...
FDA approves cure for sickle cell disease, the first ... - NBC News
WEBCasgevy, which was approved for people ages 12 and older, removes the need for a donor. Using CRISPR, it edits the DNA found in a patient’s stem cells to remove the gene that causes the disease.
FDA approves Casgevy, 1st CRISPR therapy for sickle cell disease
WEBDec 8, 2023 · The U.S. Food and Drug Administration (FDA) has approved the gene-editing therapy exagamglogene autotemcel (exa-cel) — now known as Casgevy — for treating sickle cell disease (SCD).
Casgevy: UK approves gene-editing drug for sickle cell - BBC News
WEBNov 16, 2023 · In a world first, medical regulators in the UK have approved a gene therapy that aims to cure two blood disorders. The treatment for sickle cell disease and beta thalassemia is the first to be ...
Vertex and CRISPR Therapeutics Announce Authorization of the …
WEBNov 16, 2023 · CASGEVY has been authorized for the treatment of eligible patients 12 years of age and older with SCD with recurrent vaso-occlusive crises (VOCs) or TDT, for whom a human leukocyte antigen (HLA) matched related hematopoietic stem cell donor is …
FDA approves world's first CRISPR-based medicine for sickle cell
WEBDec 8, 2023 · The new medicine, called Casgevy, is made by Vertex Pharmaceuticals and CRISPR Therapeutics. Its authorization is a scientific triumph for the technology that can efficiently and precisely repair...
Casgevy: First CRISPR gene-editing treatment approved in U.S.
WEBDec 8, 2023 · The U.S. Food and Drug Administration has approved Casgevy, the first gene-editing treatment to be marketed in the country. Casgevy uses Nobel Prize-winning technology CRISPR to treat sickle...
FDA Approves Casgevy, the First CRISPR Therapy, for Sickle Cell …
WEBDec 8, 2023 · In a truly historic decision today, the U.S. Food and Drug Administration (FDA) has, as expected, approved Casgevy, the groundbreaking CRISPR-based gene editing therapy for sickle cell disease...
The world’s first CRISPR therapy is approved: who will receive it?
WEBNov 21, 2023 · Casgevy (exagamglogene autotemcel) is a first-of-its-kind treatment made by Vertex Pharmaceuticals and CRISPR Therapeutics in Zug, Switzerland. It comes just 11 years after Jennifer Doudna and...