Axios on MSN

FDA smooths reviews of rare disease treatments

The Food and Drug Administration on Monday laid out a new pathway aimed at spurring novel individualized treatments targeting ...

FDA proposes new system for approving customized drugs and therapies for rare diseases

Federal health officials on Monday laid out a proposal to spur development of customized treatments for patients with hard-to ...

FDA accepts Beren Therapeutics’ NDA for Niemann-Pick disease

The submission includes data indicating a meaningful survival benefit for infantile-onset NPC patients treated with adrabetadex.

FDA proposes new treatment approval pathway for ultrarare diseases

The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments ...
WSKG

The FDA creates a quicker path for gene therapies

The Food and Drug Administration aims to evaluate treatments for rare diseases based on plausible evidence that they would ...

Amphastar Announces FDA Approval for Ipratropium Bromide HFA

RANCHO CUCAMONGA, CA / ACCESS Newswire / February 24, 2026 / Amphastar Pharmaceuticals, Inc. (NASDAQ:AMPH) announced that the U.S. Food and Drug Administration ("FDA") has approved the Company's ...

FDA cracks down on weight-loss drug alternatives as thousands sickened in Maryland

BALTIMORE — Popular weight-loss drugs, including Ozempic, Wegovy, Trulicity and Mounjaro, produced by independent pharmacy ...

FDA moves to facilitate personalized therapies for rare diseases

The Trump administration announced a new FDA approval pathway for individualized gene editing for rare diseases.
Texas Public Radio

FDA authorizes new drugs to treat New World screwworm in dogs and cats

The U.S. Food and Drug Administration issued two Emergency Use Authorizations for treating New World screwworm infestations ...
Opinion

How Trump’s FDA is breaking his promise to America’s patients

Months into his second term, President Donald Trump’s top health officials were clear. They promised to focus on “cures” and “meaningful treatments.” They wanted revolutionary medicine to be developed ...