Making a move, columnist Ari Anderson finds, can bring advantages but also complications that must be resolved.

With this extension, the SMA treatment Evrysdi is available for patients of all ages in Japan, from presymptomatic newborns ...

I’ve often said that it’s probably a good thing we don’t have a crystal ball. While sometimes it might be beneficial to know ...

Brianna Albers (she/her) is a crip-cyborg storyteller living in Minneapolis-St. Paul. She was diagnosed with spinal muscular atrophy type 2 in 1996 and lives with co-occurring physical and mental ...

Children with SMA type 1 treated in infancy with Zolgensma alone showed motor and lung/bulbar muscle gains over two years of ...

Differences in SMA newborn screening practices in the U.S. could impact referral patterns or the timing of therapeutic ...

Columnist Alyssa Silva found herself in unfamiliar territory when her BiPAP machine quit before bedtime, threatening her ...